Made Padmaswari MD, PhD

Made Harumi Padmaswari, MD, PhD, is a physician-scientist and researcher in gene therapy and molecular medicine, with a focus on developing innovative genome editing strategies for genetic diseases. She completed her doctoral training in Cell and Molecular Biology at the University of Arkansas, where her research centered on CRISPR-based therapeutic gene integration and its applications in muscle disorders.

Padmaswari is a recipient of the 2023 Predoctoral Fellowship in Drug Discovery from the PhRMA Foundation, recognizing her work on next-generation treatments for Duchenne muscular dystrophy (DMD). Her research aims to create durable gene therapies by integrating therapeutic genes into specific genomic sites in muscle cells, enabling long-term expression of functional proteins.

Her broader scientific contributions include studies on genome editing, exon skipping strategies, and targeted gene integration for neuromuscular diseases, advancing the field toward safer and more effective genetic therapies. Padmaswari’s work bridges clinical insight with cutting-edge biotechnology, with the goal of translating gene editing innovations into lasting treatments for patients with rare genetic disorders.