Lamya S. Shihabuddin MS, PhD

Dr. Lamya S. Shihabuddin is an accomplished leader in the biotechnology and pharmaceutical industries with over 25 years of experience skilled in building strong and productive organizations and teams. She developed a strategy and execution plan to advance multiple therapies from discovery through to early clinical development in Rare and Neurologic Diseases Therapeutic Areas. She lead and mentored cross-functional teams focused on innovative therapies and translational biomarkers for rare neurometabolic, neuromuscular and neurodegenerative diseases. She evaluated multiple external transaction opportunities and managed external academic and industrial collaborations. The managed alliance between Research, Development, and Commercial units for strategic planning.

She designed and directed research programs focused on genetics, disease mechanisms, target discovery/validation, and translational research for human genetic diseases including neuromuscular, neurometabolic, and neurodegenerative diseases. She developed targeted treatment strategies and a robust pipeline of innovative solutions using multiple therapeutic platforms including small molecules, oligonucleotides, and gene therapy. She built and integrated translational biomarkers plans to support preclinical and clinical studies. She authored numerous patents/patent applications, invited reviews, book chapters, and original research articles in major scientific journals. She served as a scientific adviser and reviewing member for Granting agencies, Advisory boards, and Consortia.