OVERVIEW

Muscular Disorders Drug Development Summit is organized by Hanson Wade and will be held from Jan 26 - 28, 2027 at Hotel Commonwealth Boston, Boston, Massachusetts, United States of America.

Description:
Strengthening Translational & Clinical Development of a New Wave of Genetic, Stem Cell, Small Molecule & RNA-Based Muscle Disease Therapies
After a year marked by uncertainty around Sarepta's Elevidys, the field is on the verge of new era shaped by cross-modality innovation and meaningful progress, with FDA submissions anticipated from Regenxbio, Capricor and Avidity that could transform therapeutic options for muscular dystrophies.

With investments including Servier’s $2.65 billion buyout of Edgewise signposting reignited pharma interest and funding opportunities, muscle disease drug developers are poised to double down on investments across their preclinical, translational and clinical programs in 2026 and beyond.

Take advantage of this timely opportunity to join 60+ industry experts spanning muscle disease biology, translation, clinical development and more at the Muscular Disorders Drug Development Summit for three days of focused collaboration designed to:

  • Explore emerging modalities beyond gene therapy
  • Discover lessons learnt from developers of approved drugs
  • Enhance biomarker measurements of muscular function and activity
  • Innovate more targeted delivery to specific muscles while avoiding off-target tissues
  • Leverage real-world data to uncover patient-relevant endpoints

With momentum building, don’t miss your chance to learn from Servier, Dyne Therapeutics, Sanofi, Biogen, Avidity Biosciences and more at the only forum dedicated to addressing biopharma’s most pressing challenges in advancing novel therapies for muscular dystrophies, Pompe disease and related myopathies.

Explore the Full Event Guide:

  • Explore the evolving cross-modality muscular disorder therapeutic landscape
  • Shape your clinical trial strategies with peer-led success stories
  • Learn how to derisk your drug development and build translational confidence
  • Investigate innovative endpoint selection tools and novel biomarkers
  • Discover expert technologies to enhance biodistribution and muscle delivery

KEY DATES

Registrations Open
31 Oct, 2026
Registrations Open
Event Start Date
26 Jan, 2027
Event Start Date
Event End Date
28 Jan, 2027
Event End Date

SPECIALITIES

Neuromuscular Medicine

SUGGESTED HOTELS

CONFERENCE VENUE

LocationHotel Commonwealth Boston
500 Commonwealth Ave